توافق إدارة الغذاء والدواء الأمريكية على أول علاج جيني قائم على الخلايا لعلاج المرضى البالغين والأطفال المصابين بالثلاسيميا بيتا والذين يحتاجون إلى عمليات نقل دم منتظمة
FDA Approves First Cell-Based Gene Therapy to Treat Adult and Pediatric Patients with Beta-thalassemia Who Require Regular Blood Transfusions
المصادر
1-
https://www.fda.gov/news-events/press-announcements/fda-approves-first-cell-based-gene-therapy-treat-adult-and-pediatric-patients-beta-thalassemia-who
2-
https://investor.bluebirdbio.com/news-releases/news-release-details/bluebird-bio-announces-launch-germany-zynteglotm-autologous-cd34
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https://www.goodrx.com/health-topic/gene-therapy/zynteglo-beta-thalassemia
4-
https://www.ema.europa.eu/en/documents/referral/zynteglo-article-20-referral-chmp-endorses-review-finding-no-link-between-viral-vector-zynteglo_en.pdf
5-
https://www.ema.europa.eu/en/medicines/human/referrals/zynteglo#:~:text=Zynteglo%20is%20a%20one%2Dtime,globin%20gene%20into%20the%20cells.